Ultragenyx

Novato, United States Founded: 2010 • Age: 16 yrs Acquired By Royalty Pharma
Therapeutics for rare and ultra-rare metabolic diseases are developed.
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About Ultragenyx

Ultragenyx is a company based in Novato (United States) founded in 2010 was acquired by Royalty Pharma in December 2019.. Ultragenyx has raised $135.1 million across 3 funding rounds from investors including Takeda Pharmaceuticals, Royalty Pharma and TPG. The company has 1,290 employees as of December 31, 2024. Ultragenyx has completed 2 acquisitions, including Dimension Therapeutics and GeneTx. Ultragenyx offers products and services including DTX401, DTX301, UX701, UX143, and GTX-102. Ultragenyx operates in a competitive market with competitors including BridgeBio, Spark Therapeutics, Alnylam, ATAI and Insitro, among others.

  • Headquarter Novato, United States
  • Employees 1290 as on 31 Dec, 2024
  • Stage Public
  • Sectors
    Healthcare
  • Email
    ***********
  • Phone
    *********
  • Website
    *********
  • Social
    *********
  • Legal Name Ultragenyx Pharmaceutical Inc.
Operational Areas
Healthcare → Biotechnology, Genomics & Life Sciences Research
Healthcare → Healthcare Products & Supplies
Healthcare → Pharmaceuticals & Therapeutics
Key Metrics
  • Annual Revenue
    $560.23 M
    29.01
    as on Dec 31, 2024
  • Net Profit
    $-569.18 M
    6.17
    as on Dec 31, 2024
  • EBITDA
    $-500.43 M
    7.87
    as on Dec 31, 2024
  • Total Equity Funding
    $135.1 M (USD)

    in 3 rounds

  • Latest Funding Round
    $75 M (USD), Series B

    Dec 31, 2012

  • Investors
  • Employee Count
    1290

    as on Dec 31, 2024

  • Investments & Acquisitions
  • Acquired by
    Royalty Pharma

    (Dec 18, 2019)

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IPO & Listings of Ultragenyx

Ultragenyx is a publicly listed company on the NASDAQ with ticker symbol RARE in USA, operating in the Health technology sector. As a publicly traded entity, the company provides investors with opportunities to participate in its growth story through equity ownership. The listing enables access to capital markets, enhances corporate visibility, and provides liquidity for shareholders while maintaining transparency through regulatory compliance and regular financial disclosures.

Exchange: NASDAQ · Ticker: RARE . Sector: Health technology · USA

Products & Services of Ultragenyx

Ultragenyx offers a comprehensive portfolio of products and services, including DTX401, DTX301, UX701, UX143, and GTX-102. The company's diverse product and service offerings are designed to meet the evolving needs of its customers, address market demands, and provide comprehensive solutions that drive value creation and customer satisfaction across various segments and use cases.

Primary

Treatment for glycogen storage disease type Ia.

Therapy for ornithine transcarbamylase deficiency.

Treatment targeting Wilson disease.

Therapy for osteogenesis imperfecta.

Treatment for Angelman syndrome.

People of Ultragenyx
Headcount 500-1000
Employee Profiles 679
Board Members and Advisors 7
Employee Profiles
People
Gabe Overbay
Executive Director, Manufacturing - Gene Therapy
People
Dennis Huang
Chief Technical Operations Officer & EVP, Gene Therapy Research & Development
People
Nataniel Ludwig
Ultra Care Liaison
People
Todd Goodrich
Senior Laboratory Equipment Technician II

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Board Members and Advisors
people
Amrit Ray
Director
people
Matthew K. Fust
Director
people
Michael Narachi
Director
people
Deborah Dunsire
Director

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Funding Insights of Ultragenyx

Ultragenyx has successfully raised a total of $135.1M across 3 strategic funding rounds. The most recent funding activity was a Series B round of $75 million completed in December 2012. This substantial capital infusion reflects strong investor confidence in the company's business model, growth potential, and market opportunities. The funding enables strategic expansion, product development, market penetration, and operational scaling to drive long-term value creation and competitive advantage.

  • Total Funding
  • Total Rounds 3
  • Last Round Series B — $75.0M
  • First Round

    (20 Jun 2011)

  • Investors Count 9
Date Amount Transaction Name Valuation Lead Investors Investors
Dec, 2012 Amount Series B - Ultragenyx Valuation Adage Capital Management
Jul, 2012 Amount Series A - Ultragenyx Valuation

investors

Jun, 2011 Amount Series A - Ultragenyx Valuation F-Prime Capital , Healthcap
Date Amount Transaction Name Valuation Lead Investors Investors
Jul, 2021 Amount Post-IPO - Grab Valuation

investors

Feb, 2021 Amount Post-IPO - Grab Valuation

investors

Jan, 2021 Amount Post-IPO - Grab Valuation

investors

Feb, 2021 Amount Post-IPO - Grab Valuation

investors

Investors in Ultragenyx

Ultragenyx has secured backing from 10 investors, including institutional and venture fund investors. Prominent investors backing the company include Takeda Pharmaceuticals, Royalty Pharma and TPG. This diverse investor base provides strategic capital, industry expertise, and valuable network connections that support the company's growth initiatives, market expansion, and long-term value creation.

All
Venture Fund
Institutional
Investor Description Founded Year Domain Location
-
Founded Year Domain Location
Fund of funds focused on pre-seed and seed-stage companies
Founded Year Domain Location
Venture capital investment and global platform support for startups.
Founded Year Domain Location
Investor Description Founded Year Domain Location
Single family office of Amitabh Bachchan, founder of Amitabh Bachchan Corporation or AB CORP
Founded Year Domain Location
Startup ecosystems are ignited through strategic investments by Signite Partners.
Founded Year Domain Location
Venture capital is directed toward companies in multiple sectors.
Founded Year Domain Location
Venture capital is invested in cybersecurity, fintech, and AI startups.
Founded Year Domain Location

Investments & Acquisitions by Ultragenyx

Ultragenyx has strategically engaged in corporate development activities, having acquired 2 companies. Notable acquisitions include Dimension Therapeutics and GeneTx. These strategic investments and acquisitions demonstrate the company's commitment to growth through portfolio expansion, market consolidation, technology integration, and strategic partnerships that enhance competitive positioning and drive long-term value creation.

Investments
Company Name Description Domain Location Founded Year Amount
Bionic investment advisor platform
2016
Fine Asian gourmet food is offered by an internet-first restaurant.
2016
Physical e-commerce kiosks are deployed for rural purchases in Indonesia.
2014
Fine Asian gourmet food is offered by an internet-first restaurant.
2016
Acquisitions
Company Name Description Domain Location Founded Year Amount
Developer of a antisense oligonucleotide for treating a rare genetic disorder
2017
Provider of gene therapy for rare diseases
2013
Company Name Description Domain Location Founded Year Amount
OVO is recognized as a smart digital payment application.
2017
Bionic investment advisor platform
2016
Physical e-commerce kiosks are deployed for rural purchases in Indonesia.
2014
Physical e-commerce kiosks are deployed for rural purchases in Indonesia.
2014

Financial Statements - Ultragenyx

Tata Steel revenue growth over time
Tata Steel profit and loss trends over time
Date Amount Transaction Name Valuation Lead Investors Investors
Jul, 2021 Amount Post-IPO - Grab Valuation

investors

Feb, 2021 Amount Post-IPO - Grab Valuation

investors

Jan, 2021 Amount Post-IPO - Grab Valuation

investors

Feb, 2021 Amount Post-IPO - Grab Valuation

investors

Ultragenyx Comparisons

Employees
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Competitors of Ultragenyx

Ultragenyx operates in a dynamic and competitive business environment, facing competition from various established players and emerging companies in the market. The competitive landscape includes prominent companies such as BridgeBio, Spark Therapeutics, Alnylam, ATAI and Insitro, among others. This competitive environment drives innovation, market differentiation, and strategic positioning as companies strive to capture market share and deliver value to their customers. Understanding the competitive dynamics is crucial for assessing market positioning, identifying growth opportunities, and navigating the challenges inherent in a competitive marketplace.

Company Name Domain Founded year HQ Location Description
domain founded_year HQ Location
Therapeutics for genetic diseases are developed through targeted interventions.
domain founded_year HQ Location
Gene therapies for rare diseases including retinal dystrophies are developed.
domain founded_year HQ Location
RNA interference-based therapeutics are developed for multiple disorders.
domain founded_year HQ Location
A biopharmaceutical company accelerating innovative mental health treatments.
domain founded_year HQ Location
An AI-enabled platform is developed for infectious disease treatment.
Company Name Domain Founded year HQ Location Description
domain founded_year HQ Location
Multiple services are booked via an app-based platform.
domain founded_year HQ Location
On-demand services are booked through an app-based platform.
domain founded_year HQ Location
App based platform offering on demand delivery and ride-hailing services
domain founded_year HQ Location
Operates an on-demand hyperlocal delivery app for food and groceries.

Frequently Asked Questions about Ultragenyx

When was Ultragenyx founded?

Ultragenyx was founded in 2010 and raised its 1st funding round 1 year after it was founded.

Where is Ultragenyx located?

Ultragenyx is headquartered in Novato, United States. It is registered at Novato, California, United States.

Is Ultragenyx a funded company?

Ultragenyx is a funded company, having raised a total of $135.1M across 3 funding rounds to date. The company's 1st funding round was a Series A of $45M, raised on Jun 20, 2011.

How many employees does Ultragenyx have?

As of Dec 31, 2024, the latest employee count at Ultragenyx is 1,290.

What is the annual revenue of Ultragenyx?

Annual revenue of Ultragenyx is $560.23M as on Dec 31, 2024.

What does Ultragenyx do?

The company was founded in 2010 and is headquartered in Novato, United States, within the biotechnology sector. Focus is placed on developing treatments for rare and ultra-rare metabolic disorders. Burosumab, a fully human monoclonal antibody, is indicated for X-linked hypophosphatemia and tumor-induced osteomalacia. rhGUS (UX003), a recombinant enzyme, is advanced for mucopolysaccharidosis 7, a lysosomal storage disease. Operations center on clinical-stage pipeline advancement for these conditions.

Who are the top competitors of Ultragenyx?

Ultragenyx's top competitors include Spark Therapeutics, BridgeBio and Forge Biologics.

What products or services does Ultragenyx offer?

Ultragenyx offers DTX401, DTX301, UX701, UX143, and GTX-102.

Is Ultragenyx publicly traded?

Yes, Ultragenyx is publicly traded on NASDAQ under the ticker symbol RARE.

How many acquisitions has Ultragenyx made?

Ultragenyx has made 2 acquisitions, including Dimension Therapeutics, and GeneTx.

Who are Ultragenyx's investors?

Ultragenyx has 10 investors. Key investors include Takeda Pharmaceuticals, Royalty Pharma, TPG, T. Rowe Price, and Eight Roads Ventures.

What is Ultragenyx's ticker symbol?

The ticker symbol of Ultragenyx is RARE on NASDAQ.

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